Taysha Gene Therapies Inc. (NASDAQ:TSHA) is one of the best penny stocks to buy for 2026. On January 6, the company confirmed ...
Rett syndrome is a neurodevelopmental disorder that primarily affects girls, most of whom have mutations in the transcription regulatory gene MECP2. However, mutations in MECP2 also have been ...
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New discoveries about the severe developmental disorder known as Rett syndrome could open the door to better treatments for the devastating, life-shortening condition. Scientists investigating the ...
Neurogene Inc. (Nasdaq: NGNE), a clinical-stage company founded to bring life-changing genetic medicines to patients and families affected by rare neurological diseases, today provided an update on ...
UAB will study a drug originally developed for Parkinson’s disease that may help reduce breath holding in patients with Rett syndrome. Pediatric neurologist Alan Percy, M.D., is a leading clinician ...
We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Health Canada has approved Daybue to treat Rett syndrome ...
Rett syndrome is a rare disorder linked to autism that affects brain development. Microglia, the resident immune cells of the central nervous system, have been implicated in the development of Rett ...
First patient dosed in REVEAL pivotal trial evaluating TSHA-102 (N=15, aged 6 to <22 years) in Q4 2025, with enrollment advancing across ...
Neurogene Gene Therapy Shows Signs of Efficacy in Small Study, But an Adverse Event Spooks Investors
A Neurogene gene therapy in development for the rare neurodevelopmental disorder Rett syndrome has encouraging early data in a small group of patients, an interim readout that comes a week after a ...
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