Casgevy gene therapy for UK children was extended to patients aged five and over by the MHRA on October 29, 2026; a milestone ...

Players: Pfizer, Novartis, Bayer, Astellas and Sarepta. Profile: next-gen AAV delivery, including engineered capsids, targeting, safety and scalable manufacturing.Dublin, Oct. 30, 2026 (GLOBE NEWSWIRE ...

Indian American couple’s gift will help combine genetic research with nanotechnology to develop more effective gene therapies ...

In a phase 2 study, SAR402663 gene therapy for wet age-related macular degeneration showed positive efficacy and safety ...

MassHealth's Katelyn Meyer, Pharm.D., says mandatory coverage, young patients and an unpredictable FDA make planning for new ...

Dual vector and AAV.SPR technologies combine to drive supraphysiological levels of full-length MYO7A in non-human primate retina, reaching the macula without foveal detachmentSix-month GLP toxicology ...

In recent months, news came out about several distressing cases that have underscored the risks of gene therapy, which delivers DNA to a patient’s cells to treat disease. All of these cases have one ...

Genprex, Inc. announced that research conducted under its sponsored research collaboration with Meharry Medical College will ...

Cardiologists who study gene therapy explain its promise, risks and the safeguards needed for responsible use.

Therapy pioneered by biotechnology Chinese firm HuidaGene showed promise in animals but caused a fatal reaction in a child.

Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...

Optogenetics, recognized by the 2026 medicine Nobel, makes cells respond to light, including eye cells that normally relay ...