Cardiologists who study gene therapy explain its promise, risks and the safeguards needed for responsible use.

Genprex, Inc. announced that research conducted under its sponsored research collaboration with Meharry Medical College will ...

Gene therapy cut severe infections 93% in Wiskott-Aldrich syndrome, using patients’ own modified stem cells to treat a rare ...

After decades developing gene therapies for ultra-rare conditions, Alessandra Biffi is researching how altering a patient’s ...

In recent months, news came out about several distressing cases that have underscored the risks of gene therapy, which ...

New data showing rapid and durable full-length MECP2 expression in vivo with single-stranded AAV support improvements ...

Gene therapy is no longer the future of medicine—it's reality. Treatments that replace, silence or edit genes are already ...

MarketsandMarkets™ projects the global gene therapy market, valued at USD 7.21 billion in 2023 and USD 8.85 billion in 2024, ...

Elizabeth "Liz" Parrish, founder and CEO of BioViva Sciences USA Inc., announces the release of her new book, How I Became a GMO and Why You Will Too: A Manifesto for Human Longevity. Blending ...

Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...

“It’s something that we would have never really expected to happen in our career, for kids to be able to hear without the ...

Researchers at the University of Cincinnati College of Medicine have published the first proof-of-concept study showing the potential of an experimental gene therapy for hydrocephalus. The preclinical ...